Clinical trials & development

Miplyffa bags FDA approval for ultra-rare disease

FDA greenlights first treatment for Niemann-Pick disease type C

By Jonathan Smith

The small molecule drug arimoclomol (Miplyffa) has got the green light from the U.S. Food and Drug Administration (FDA) for the treatment of the rare disease Niemann-Pick disease type C (NPC), which until now has lacked FDA-approved therapies.

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Phastar's RBQM app enhances clinical trial data monitoring

By Liza Laws

Phastar have implemented an RBQM app within their Clinical Intelligence Data Visualisation Platform, enabling a comprehensive overview of the entire trial across all sites which can be shown in various visualisation graphs, tailored by client.

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AI-driven insights: SOMS boosts clinical trial success

By Liza Laws

In an in-depth conversation, OSP senior editor, Liza Laws, interviews Adrian Kizewski, associate director at IQVIA, to uncover the transformative impact of the Sub-population Optimization & Modeling Solution (SOMS) on clinical trials.

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Reimagine Care and Memorial Hermann boost cancer care engagement

By Liza Laws

Reimagine Care, the leading provider of on-demand cancer care, and Memorial Hermann Health System, one of Texas's largest not-for-profit health systems, have announced an ambitious multi-year expansion of their pioneering partnership.

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