Duchenne foundation funds research leading to first-in-human clinical study
The research taking place at Nationwide Children’s Hospital is seeking a treatment for a rare Duchenne muscular dystrophy mutation.
Archives for August 19, 2020
Cerba Research: collaboration boosts rare-disease discoveries
A leader from the clinical laboratory and diagnostic solution provider discusses how its research is fueled by partnerships and patient-centricity.
Healx collaborates on Angelman syndrome therapies
The AI-centric drug discovery technology firm is working with a foundation to discover potential treatments for the rare neurogenetic disorder.
Drug discovery platform aims to accelerate rare-disease therapies
An online patient community specializing in rare diseases has launched Xperiome, a knowledge platform aimed at speeding development of treatments.
Biorasi: precision medicine trials call for specialized approach
A leader from the speed-focused CRO talks about the specialized needs of precision medicine trials, and how sites and sponsors can succeed on such studies.
Notable, Washington University join on oncology study
The precision study at the center of the partnership is geared toward identifying novel synergies across a broad variety of anticancer therapies.